Our Fellowship provides training for clinician scientists in the field of pediatric genetic therapies and personalized medicine.  At the end of training, the specific goals are that all trainees will: Be conversant with modern molecular therapeutic approaches. Have completed IRB-certified training in Human Subjects Research. Have participated in the performance of at least one pre-clinical (laboratory-based) study of novel therapeutics. Understand utility, limitations, and application of genomic testing and follow-up in pediatric patients. Have participated in the design, initiation, performance, and/or interpretation of at least one clinical trial of genetic therapeutics. Write and submit an NIH K08, K23, or equivalent fo